Paving the way for future gene therapies: A case study of scientific spillover from delandistrogene moxeparvovec

Paving the way for future gene therapies: A case study of scientific spillover from delandistrogene moxeparvovec

Gene therapies have potential to improve outcomes of severe diseases after only a single administration. Novel therapies are continually being developed using knowledge gained from prior successes, a concept known as scientific spillover. Gene therapy advancement requires extensive development at ea...

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Bibliographic Details
Main Authors:	Damon Asher, Daisy Dai, Alexa C. Klimchak, Lauren E. Sedita, Katherine L. Gooch, Louise Rodino-Klapac
Format:	Article
Language:	English
Published:	Elsevier 2023-09-01
Series:	Molecular Therapy: Methods & Clinical Development
Subjects:	delandistrogene moxeparvovec Duchenne muscular dystrophy gene therapy rare disease scientific spillover SRP-9001
Online Access:	http://www.sciencedirect.com/science/article/pii/S232905012300116X

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