Drug Repurposing and Lysosomal Storage Disorders: A Trick to Treat

Drug Repurposing and Lysosomal Storage Disorders: A Trick to Treat

Rare diseases, or orphan diseases, are defined as diseases affecting a small number of people compared to the general population. Among these, we find lysosomal storage disorders (LSDs), a cluster of rare metabolic diseases characterized by enzyme mutations causing abnormal glycolipid storage. Drug...

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Bibliographic Details
Main Authors:	Bruno Hay Mele, Federica Rossetti, Maria Vittoria Cubellis, Maria Monticelli, Giuseppina Andreotti
Format:	Article
Language:	English
Published:	MDPI AG 2024-02-01
Series:	Genes
Subjects:	lysosomal storage disease lysosomal storage disorder lysosomal enzyme disorder drug repositioning drug repurposing
Online Access:	https://www.mdpi.com/2073-4425/15/3/290

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