Clinical Efficacy and Safety of Ivacaftor/Lumacaftor Combination in Patients with Cystic Fibrosis: International Studies Review
Cystic fibrosis is an autosomal recessive disease caused by structure abnormalities in the cystic fibrosis transmembrane conductance regulator (CFTR) gene. It is characterized by severe course and poor prognosis without or with insufficient treatment. Approval of pathogenetic therapy medications, CF...
| Main Authors: | , , |
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| Formato: | Artigo |
| Idioma: | English |
| Publicado: |
"Paediatrician" Publishers LLC
2021-12-01
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| Series: | Вопросы современной педиатрии |
| Subjects: | |
| Acceso en liña: | https://vsp.spr-journal.ru/jour/article/view/2794 |