Allogeneic hematopoietic stem cell transplantation for treating severe lung involvement in Gaucher disease
Objective: To provide strategies for monitoring and treating severe lung involvement in Gaucher disease. Study design: We reviewed the chart of a 5-year-old boy who developed rapidly progressive, severe infiltrative lung involvement of Gaucher disease (GD) and improved after allogeneic hematopoietic...
Main Authors: | Fu-Shiuan Lee, Hsiu-Ju Yen, Dau-Ming Niu, Giun-Yi Hung, Chih-Ying Lee, Yi-Chen Yeh, Paul Chih-Hsueh Chen, Sheng-Kai Chang, Chia-Feng Yang |
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Format: | Article |
Language: | English |
Published: |
Elsevier
2020-12-01
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Series: | Molecular Genetics and Metabolism Reports |
Subjects: | |
Online Access: | http://www.sciencedirect.com/science/article/pii/S2214426920300987 |
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