The Role of Hematopoietic Cell Transplant in the Glycoprotein Diseases

The Role of Hematopoietic Cell Transplant in the Glycoprotein Diseases

The glycoprotein disorders are a group of lysosomal storage diseases (α-mannosidosis, aspartylglucosaminuria, β-mannosidosis, fucosidosis, galactosialidosis, sialidosis, mucolipidosis II, mucolipidosis III, and Schindler Disease) characterized by specific lysosomal enzyme defects and resultant build...

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Bibliographic Details
Main Authors:	Brianna M. Naumchik, Ashish Gupta, Heather Flanagan-Steet, Richard A. Steet, Sara S. Cathey, Paul J. Orchard, Troy C. Lund
Format:	Article
Language:	English
Published:	MDPI AG 2020-06-01
Series:	Cells
Subjects:	glycoprotein disorders lysosomal storage disease hematopoietic cell transplant enzyme replacement therapy α-mannosidosis aspartylglucosaminuria
Online Access:	https://www.mdpi.com/2073-4409/9/6/1411

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