P1588: LONG-TERM REAL-WORLD EFFECTIVENESS OF ELIGLUSTAT IN TREATMENT-NAÏVE AND SWITCH PATIENTS ENROLLED IN THE INTERNATIONAL COLLABORATIVE GAUCHER GROUP (ICGG) GAUCHER REGISTRY
| Main Authors: | , , , , , , , |
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| Format: | Article |
| Language: | English |
| Published: |
Wiley
2023-08-01
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| Series: | HemaSphere |
| Online Access: | http://journals.lww.com/10.1097/01.HS9.0000973228.21913.33 |
| _version_ | 1797280187316961280 |
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| author | Pramod Mistry Manisha Balwani Joel Charrow Jeremy Lorber Claus Niederau Jenny Carwile Sefika Uslu Priya S. Kishnani |
| author_facet | Pramod Mistry Manisha Balwani Joel Charrow Jeremy Lorber Claus Niederau Jenny Carwile Sefika Uslu Priya S. Kishnani |
| author_sort | Pramod Mistry |
| collection | DOAJ |
| first_indexed | 2024-03-07T16:36:27Z |
| format | Article |
| id | doaj.art-86d87eaa776442bdb54fa0be6dfd098b |
| institution | Directory Open Access Journal |
| issn | 2572-9241 |
| language | English |
| last_indexed | 2024-03-07T16:36:27Z |
| publishDate | 2023-08-01 |
| publisher | Wiley |
| record_format | Article |
| series | HemaSphere |
| spelling | doaj.art-86d87eaa776442bdb54fa0be6dfd098b2024-03-03T09:43:22ZengWileyHemaSphere2572-92412023-08-017e219133310.1097/01.HS9.0000973228.21913.33202308003-01481P1588: LONG-TERM REAL-WORLD EFFECTIVENESS OF ELIGLUSTAT IN TREATMENT-NAÏVE AND SWITCH PATIENTS ENROLLED IN THE INTERNATIONAL COLLABORATIVE GAUCHER GROUP (ICGG) GAUCHER REGISTRYPramod Mistry0Manisha Balwani1Joel Charrow2Jeremy Lorber3Claus Niederau4Jenny Carwile5Sefika Uslu6Priya S. Kishnani71 Yale University School of Medicine, New Haven, United States2 Icahn School of Medicine at Mount Sinai, Department of Genetics and Genomic Sciences, New York, United States3 Ann & Robert H Lurie Children’s Hospital of Chicago, Chicago, United States4 Cedars-Sinai Medical Center, Los Angeles, California, United States5 Katholisches Klinikum Oberhausen, Department of Medicine, Oberhausen, Germany6 Sanofi, Rare Disease, Epidemiology and Biostatistics, Cambridge, MA, United States7 Sanofi, Rare Hematology, Cambridge, MA, United States8 Duke University, Division of Medical Genetics, Department of Pediatrics, Durham, North Carolina, United Stateshttp://journals.lww.com/10.1097/01.HS9.0000973228.21913.33 |
| spellingShingle | Pramod Mistry Manisha Balwani Joel Charrow Jeremy Lorber Claus Niederau Jenny Carwile Sefika Uslu Priya S. Kishnani P1588: LONG-TERM REAL-WORLD EFFECTIVENESS OF ELIGLUSTAT IN TREATMENT-NAÏVE AND SWITCH PATIENTS ENROLLED IN THE INTERNATIONAL COLLABORATIVE GAUCHER GROUP (ICGG) GAUCHER REGISTRY HemaSphere |
| title | P1588: LONG-TERM REAL-WORLD EFFECTIVENESS OF ELIGLUSTAT IN TREATMENT-NAÏVE AND SWITCH PATIENTS ENROLLED IN THE INTERNATIONAL COLLABORATIVE GAUCHER GROUP (ICGG) GAUCHER REGISTRY |
| title_full | P1588: LONG-TERM REAL-WORLD EFFECTIVENESS OF ELIGLUSTAT IN TREATMENT-NAÏVE AND SWITCH PATIENTS ENROLLED IN THE INTERNATIONAL COLLABORATIVE GAUCHER GROUP (ICGG) GAUCHER REGISTRY |
| title_fullStr | P1588: LONG-TERM REAL-WORLD EFFECTIVENESS OF ELIGLUSTAT IN TREATMENT-NAÏVE AND SWITCH PATIENTS ENROLLED IN THE INTERNATIONAL COLLABORATIVE GAUCHER GROUP (ICGG) GAUCHER REGISTRY |
| title_full_unstemmed | P1588: LONG-TERM REAL-WORLD EFFECTIVENESS OF ELIGLUSTAT IN TREATMENT-NAÏVE AND SWITCH PATIENTS ENROLLED IN THE INTERNATIONAL COLLABORATIVE GAUCHER GROUP (ICGG) GAUCHER REGISTRY |
| title_short | P1588: LONG-TERM REAL-WORLD EFFECTIVENESS OF ELIGLUSTAT IN TREATMENT-NAÏVE AND SWITCH PATIENTS ENROLLED IN THE INTERNATIONAL COLLABORATIVE GAUCHER GROUP (ICGG) GAUCHER REGISTRY |
| title_sort | p1588 long term real world effectiveness of eliglustat in treatment naive and switch patients enrolled in the international collaborative gaucher group icgg gaucher registry |
| url | http://journals.lww.com/10.1097/01.HS9.0000973228.21913.33 |
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