Laboratory Tools to Predict CFTR Modulator Therapy Effectiveness and to Monitor Disease Severity in Cystic Fibrosis

Laboratory Tools to Predict CFTR Modulator Therapy Effectiveness and to Monitor Disease Severity in Cystic Fibrosis

The implementation of cystic fibrosis (CF) transmembrane conductance regulator (CFTR) modulator drugs into clinical practice has been attaining remarkable therapeutic outcomes for CF, a life-threatening autosomal recessive genetic disease. However, there is elevated CFTR allelic heterogeneity, and v...

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Bibliographic Details
Main Authors: Mafalda Bacalhau, Mariana Camargo, Miquéias Lopes-Pacheco
Format: Article
Language:English
Published: MDPI AG 2024-01-01
Series:Journal of Personalized Medicine
Subjects:
airway cells
bioassay
biomarkers
extracellular vesicles
inflammation
microRNA
Online Access:https://www.mdpi.com/2075-4426/14/1/93

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