P028: Improved neurocognitive outcomes in neuronopathic mucopolysaccharidosis type II: A case of early hematopoietic stem cell transplant
Main Authors: | Emma Michl, Benjamin Goodlett, Christine Duncan, Olaf Bodamer |
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Format: | Article |
Language: | English |
Published: |
Elsevier
2023-01-01
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Series: | Genetics in Medicine Open |
Online Access: | http://www.sciencedirect.com/science/article/pii/S2949774423000389 |
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