Gene therapy and genome editing for primary immunodeficiency diseases

Gene therapy and genome editing for primary immunodeficiency diseases

In past two decades the gene therapy using genetic modified autologous hematopoietic stem cells (HSCs) transduced with the viral vector has become a promising alternative option for treating primary immunodeficiency diseases (PIDs). Despite of some pitfalls at early stage clinical trials, the field...

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Bibliographic Details
Main Authors:	Zhi-Yong Zhang, Adrian J. Thrasher, Fang Zhang
Format:	Article
Language:	English
Published:	KeAi Communications Co., Ltd. 2020-03-01
Series:	Genes and Diseases
Online Access:	http://www.sciencedirect.com/science/article/pii/S2352304219300510

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