Intravitreal injection of new adeno-associated viral vector: Enhancing retinoschisin 1 gene transduction in a mouse model of X-linked retinoschisis

Adeno-associated virus (AAV) vectors have been widely used in therapy to treat hereditary retinal diseases. But its transduction efficiency by intravitreal injection still needs to be improved. In this study, we investigated the transduction efficiency of AAV-DJ (K137R)-GFP in different retinal cell...

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Bibliographic Details
Main Authors: Yan Sun, Dan Xiao, Zhuang Li, Dan Xu, Donglei Zhang, Yuanlong An, Jinyue Xue, Yue Ren, Shu Liu, Di Wang, Jun Li, Zhuoshi Wang, Jijing Pang
Format: Article
Language:English
Published: Elsevier 2024-03-01
Series:Biochemistry and Biophysics Reports
Online Access:http://www.sciencedirect.com/science/article/pii/S2405580824000104