Recent Advances in Gene Therapy for Familial Hypercholesterolemia: An Update Review

Recent Advances in Gene Therapy for Familial Hypercholesterolemia: An Update Review

(1) Background: Existing lipid-lowering therapies have difficulty in achieving lipid target levels in patients with familial hypercholesterolemia (FH), especially in the treatment of patients with homozygous familial hypercholesterolemia. (2) Method: All of the literature data containing “Familial h...

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Bibliographic Details
Main Authors:	Qingan Fu, Lijuan Hu, Tianzhou Shen, Renqiang Yang, Long Jiang
Format:	Article
Language:	English
Published:	MDPI AG 2022-11-01
Series:	Journal of Clinical Medicine
Subjects:	familial hypercholesterolemia antisense oligonucleotide small interfering RNA CRISPR/Cas9 gene therapy
Online Access:	https://www.mdpi.com/2077-0383/11/22/6773

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