Safety and effectiveness of taliglucerase alfa in patients with Gaucher disease: an interim analysis of real-world data from a multinational drug registry (TALIAS)

Safety and effectiveness of taliglucerase alfa in patients with Gaucher disease: an interim analysis of real-world data from a multinational drug registry (TALIAS)

Abstract Background Limited real-world data from routine clinical care are available on the safety and effectiveness of treatment with taliglucerase alfa in patients with Gaucher disease (GD). Methods Taliglucerase Alfa Surveillance (TALIAS), a multinational prospective Drug Registry of patients wit...

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Bibliografische gegevens
Hoofdauteurs: Lina Titievsky, Tilman Schuster, Ronnie Wang, Muhammad Younus, Andrew Palladino, Kabir Quazi, Michael P. Wajnrajch, Betina Hernandez, Pamela S. Becker, Neal J. Weinreb, Christina Chambers, Roy Mansfield, Louise Taylor, Li-Jung Tseng, Paige Kaplan
Formaat: Artikel
Taal:English
Gepubliceerd in: BMC 2022-04-01
Reeks:Orphanet Journal of Rare Diseases
Onderwerpen:
Taliglucerase alfa
Gaucher disease
Effectiveness
Non-interventional study
Safety
Online toegang:https://doi.org/10.1186/s13023-022-02289-7

Internet

https://doi.org/10.1186/s13023-022-02289-7

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