Promise of gene therapy for congenital neurologic disease due to GPI deficiency

Promise of gene therapy for congenital neurologic disease due to GPI deficiency

Bibliographic Details
Main Authors:	Daria V. Babushok, Denise E. Sabatino
Format:	Article
Language:	English
Published:	Elsevier 2024-06-01
Series:	Molecular Therapy: Methods & Clinical Development
Online Access:	http://www.sciencedirect.com/science/article/pii/S2329050124000561

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