Betibeglogene Autotemcel; A new hope for transfusion dependent beta-thalassaemia
Respected Editor, Beta thalassaemia is an autosomal recessive disorder that leads to abnormal production of functional adult haemoglobin because of either inadequate or absent production of the B globin chain (beta+/beta0).1 Transfusion-dependent thalassemia (TDT) is a rare and most severe form req...
Main Authors: | Hiba Tariq Wally, Muhammad Hassan Zulfi, Elahi Sana Jilani |
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Format: | Article |
Language: | English |
Published: |
Pakistan Medical Association
2023-09-01
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Series: | Journal of the Pakistan Medical Association |
Online Access: | https://ojs.jpma.org.pk/index.php/public_html/article/view/9532 |
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