Long-term dystrophin restoration supports development of splice correction therapy for DMD patients with exon 2 duplications
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| Format: | Article |
| Language: | English |
| Published: |
Elsevier
2023-12-01
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| Series: | Molecular Therapy: Methods & Clinical Development |
| Online Access: | http://www.sciencedirect.com/science/article/pii/S2329050123001997 |