CRISPR medicine for blood disorders: Progress and challenges in delivery

CRISPR medicine for blood disorders: Progress and challenges in delivery

Blood disorders are a group of diseases including hematological neoplasms, clotting disorders and orphan immune deficiency diseases that affects human health. Current improvements in genome editing based therapeutics demonstrated preclinical and clinical proof to treat different blood disorders. Gen...

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Bibliographic Details
Main Authors:	Tahereh Mohammadian Gol, Guillermo Ureña-Bailén, Yujuan Hou, Ralph Sinn, Justin S. Antony, Rupert Handgretinger, Markus Mezger
Format:	Article
Language:	English
Published:	Frontiers Media S.A. 2023-01-01
Series:	Frontiers in Genome Editing
Subjects:	CRISPR/Cas blood disorder physical delivery viral vectors non-viral vectors
Online Access:	https://www.frontiersin.org/articles/10.3389/fgeed.2022.1037290/full

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