Natural history of Duchenne muscular dystrophy in the United Kingdom: A descriptive study using the Clinical Practice Research Datalink

Abstract Background Duchenne muscular dystrophy (DMD) is a rare, muscle‐degenerative disease predominantly affecting males. Natural history models capture the full disease pathway under current care and combine with estimates of new interventions’ effects to assess cost‐effectiveness by health techn...

وصف كامل

التفاصيل البيبلوغرافية
المؤلفون الرئيسيون: Jonathan Broomfield, Keith Abrams, Nick Latimer, Michela Guglieri, Mark Rutherford, Michael Crowther
التنسيق: مقال
اللغة:English
منشور في: Wiley 2023-12-01
سلاسل:Brain and Behavior
الموضوعات:
الوصول للمادة أونلاين:https://doi.org/10.1002/brb3.3331