Current and Future Perspective in Hematopoietic Stem Progenitor Cell-gene Therapy for Inborn Errors of Metabolism

Bibliographic Details
Main Authors: Francesca Tucci, Giulia Consiglieri, Matilde Cossutta, Maria Ester Bernardo
Format: Article
Language:English
Published: Wiley 2023-10-01
Series:HemaSphere
Online Access:http://journals.lww.com/10.1097/HS9.0000000000000953