Emicizumab in children: bleeding episodes and outcome before and after transition to Emicizumab

Emicizumab in children: bleeding episodes and outcome before and after transition to Emicizumab

Abstract Purpose Real-world data and study data regarding therapy with Emicizumab in pediatric cohorts with haemophilia A is scarce. Especially, data on previously untreated pediatric patients (PUPs) and minimally treated patients (MTPs) are missing. Methods Thirteen pediatric patients with haemophi...

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Bibliographic Details
Main Authors: Hannah Glonnegger, Felicia Andresen, Friedrich Kapp, Stefano Malvestiti, Martin Büchsel, Barbara Zieger
Format: Article
Language:English
Published: BMC 2022-08-01
Series:BMC Pediatrics
Subjects:
Emicizumab
Hemlibra
Children
Annual bleeding rate
Online Access:https://doi.org/10.1186/s12887-022-03546-1

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