Hematopoietic Stem Cell Transplantation in <i>CSF1R</i>-Related Leukoencephalopathy: Retrospective Study on Predictors of Outcomes

Hematopoietic Stem Cell Transplantation in <i>CSF1R</i>-Related Leukoencephalopathy: Retrospective Study on Predictors of Outcomes

Mutations in the <i>CSF1R</i> gene are the most common cause of adult-onset leukoencephalopathy with axonal spheroids and pigmented glia (ALSP), a neurodegenerative disease with rapid progression and ominous prognosis. Hematopoietic stem cell transplantation (HSCT) has been increasingly...

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Bibliographic Details
Main Authors: Jarosław Dulski, Michael G. Heckman, Launia J. White, Kamila Żur-Wyrozumska, Troy C. Lund, Zbigniew K. Wszolek
Format: Article
Language:English
Published: MDPI AG 2022-12-01
Series:Pharmaceutics
Subjects:
adult-onset
axonal spheroids
pigmented glia
ALSP
HSCT
bone marrow transplant
Online Access:https://www.mdpi.com/1999-4923/14/12/2778

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