Targeted <i>SMN</i> Exon Skipping: A Useful Control to Assess In Vitro and In Vivo Splice-Switching Studies

The literature surrounding the use of antisense oligonucleotides continues to grow, with new disease and mechanistic applications constantly evolving. Furthermore, the discovery and advancement of novel chemistries continues to improve antisense delivery, stability and effectiveness. For each new ap...

पूर्ण विवरण

ग्रंथसूची विवरण
मुख्य लेखकों: Loren L. Flynn, Chalermchai Mitrpant, Abbie Adams, Ianthe L. Pitout, Anja Stirnweiss, Sue Fletcher, Steve D. Wilton
स्वरूप: लेख
भाषा:English
प्रकाशित: MDPI AG 2021-05-01
श्रृंखला:Biomedicines
विषय:
ऑनलाइन पहुंच:https://www.mdpi.com/2227-9059/9/5/552