Real-world data assessment of safety of home-based and hospital/outpatient-based laronidase enzyme replacement therapy for mucopolysaccharidosis I
| Main Authors: | , , |
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| Format: | Article |
| Language: | English |
| Published: |
Elsevier
2021-06-01
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| Series: | Molecular Genetics and Metabolism Reports |
| Subjects: | |
| Online Access: | http://www.sciencedirect.com/science/article/pii/S2214426921000306 |
| _version_ | 1818950533990318080 |
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| author | Amanda Wilson Raffaella M. Colzani Ana Lorena Flores |
| author_facet | Amanda Wilson Raffaella M. Colzani Ana Lorena Flores |
| author_sort | Amanda Wilson |
| collection | DOAJ |
| first_indexed | 2024-12-20T09:20:07Z |
| format | Article |
| id | doaj.art-c7c806c8fa3a414d8f886cb8f72cfe25 |
| institution | Directory Open Access Journal |
| issn | 2214-4269 |
| language | English |
| last_indexed | 2024-12-20T09:20:07Z |
| publishDate | 2021-06-01 |
| publisher | Elsevier |
| record_format | Article |
| series | Molecular Genetics and Metabolism Reports |
| spelling | doaj.art-c7c806c8fa3a414d8f886cb8f72cfe252022-12-21T19:45:19ZengElsevierMolecular Genetics and Metabolism Reports2214-42692021-06-0127100736Real-world data assessment of safety of home-based and hospital/outpatient-based laronidase enzyme replacement therapy for mucopolysaccharidosis IAmanda Wilson0Raffaella M. Colzani1Ana Lorena Flores2Corresponding author.; Sanofi Genzyme, USASanofi Genzyme, USASanofi Genzyme, USAhttp://www.sciencedirect.com/science/article/pii/S2214426921000306Real-world evidenceenzyme replacement therapyMPS IHome-based infusion |
| spellingShingle | Amanda Wilson Raffaella M. Colzani Ana Lorena Flores Real-world data assessment of safety of home-based and hospital/outpatient-based laronidase enzyme replacement therapy for mucopolysaccharidosis I Molecular Genetics and Metabolism Reports Real-world evidence enzyme replacement therapy MPS I Home-based infusion |
| title | Real-world data assessment of safety of home-based and hospital/outpatient-based laronidase enzyme replacement therapy for mucopolysaccharidosis I |
| title_full | Real-world data assessment of safety of home-based and hospital/outpatient-based laronidase enzyme replacement therapy for mucopolysaccharidosis I |
| title_fullStr | Real-world data assessment of safety of home-based and hospital/outpatient-based laronidase enzyme replacement therapy for mucopolysaccharidosis I |
| title_full_unstemmed | Real-world data assessment of safety of home-based and hospital/outpatient-based laronidase enzyme replacement therapy for mucopolysaccharidosis I |
| title_short | Real-world data assessment of safety of home-based and hospital/outpatient-based laronidase enzyme replacement therapy for mucopolysaccharidosis I |
| title_sort | real world data assessment of safety of home based and hospital outpatient based laronidase enzyme replacement therapy for mucopolysaccharidosis i |
| topic | Real-world evidence enzyme replacement therapy MPS I Home-based infusion |
| url | http://www.sciencedirect.com/science/article/pii/S2214426921000306 |
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