Effects of Sirolimus Treatment on Fetal Hemoglobin Production and Response to SARS-CoV-2 Vaccination: A Case Report Study
The β-thalassemias are a group of monogenic hereditary hematological disorders caused by deletions and/or mutations of the β-globin gene, leading to low or absent production of adult hemoglobin (HbA). For β-thalassemia, sirolimus has been under clinical consideration in two trials (NCT03877809 and N...
Main Authors: | Maria Rita Gamberini, Cristina Zuccato, Matteo Zurlo, Lucia Carmela Cosenza, Alessia Finotti, Roberto Gambari |
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Format: | Article |
Language: | English |
Published: |
MDPI AG
2023-07-01
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Series: | Hematology Reports |
Subjects: | |
Online Access: | https://www.mdpi.com/2038-8330/15/3/44 |
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