Drug repurposing for rare: progress and opportunities for the rare disease community

Drug repurposing for rare: progress and opportunities for the rare disease community

Repurposing is one of the key opportunities to address the unmet rare diseases therapeutic need. Based on cases of drug repurposing in small population conditions, and previous work in drug repurposing, we analyzed the most important lessons learned, such as the sharing of clinical observations, rea...

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Bibliographic Details
Main Authors: Anneliene Hechtelt Jonker, Daniel O’Connor, Maria Cavaller-Bellaubi, Christine Fetro, Maria Gogou, Peter A. C. ’T Hoen, Martin de Kort, Heather Stone, Nivedita Valentine, Anna Maria Gerdina Pasmooij
Format: Article
Language:English
Published: Frontiers Media S.A. 2024-01-01
Series:Frontiers in Medicine
Subjects:
drug repurposing
rare diseases
orphan drugs
unmet need
innovation
therapy development
Online Access:https://www.frontiersin.org/articles/10.3389/fmed.2024.1352803/full

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