Development and recent progresses of gene therapy for β-thalassemia
β-thalassemias are among the most common inherited monogenic disorders worldwide due to mutations in the β-globin gene that reduce or abolish the production of the β-globin chain resulting in transfusion-dependent chronic anemia. Currently, the only curative treatment is allogeneic hematopoietic ste...
| Auteurs principaux: | , , , , , |
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| Format: | Article |
| Langue: | English |
| Publié: |
MDPI AG
2014-09-01
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| Collection: | Thalassemia Reports |
| Sujets: | |
| Accès en ligne: | http://www.pagepressjournals.org/index.php/thal/article/view/2925 |