Investigation of the bone damage in mucopolysaccharidosis type I Hurler Syndrome: Pathophysiological mechanisms and the impact of ex vivo gene therapy

Investigation of the bone damage in mucopolysaccharidosis type I Hurler Syndrome: Pathophysiological mechanisms and the impact of ex vivo gene therapy

Bibliographic Details
Main Authors:	Sara Penna, Stefania Crippa, Valentina Capo, Ludovica Santi, Roberto Bosotti, Mara Riminucci, Alessandro Corsi, Marta Serafini, Bernhard Gentner, Alessandro Aiuti, Maria Ester Bernardo, Anna Villa
Format:	Article
Language:	English
Published:	Elsevier 2020-10-01
Series:	Bone Reports
Online Access:	http://www.sciencedirect.com/science/article/pii/S2352187220303570

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