O30: REKLAIM: A first in human phase Ib clinical trial of FBX-101 (AAVrh10.GALC) intravenously administered after UCBT for infantile Krabbe disease
| Main Authors: | , , , , , |
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| Format: | Article |
| Language: | English |
| Published: |
Elsevier
2024-01-01
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| Series: | Genetics in Medicine Open |
| Online Access: | http://www.sciencedirect.com/science/article/pii/S2949774424000219 |
| _version_ | 1797267637111095296 |
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| author | Maria Escolar Mark Vander Lugt Raymond Wang Juan Ruiz Michele Poe Paul Szabolcs |
| author_facet | Maria Escolar Mark Vander Lugt Raymond Wang Juan Ruiz Michele Poe Paul Szabolcs |
| author_sort | Maria Escolar |
| collection | DOAJ |
| first_indexed | 2024-04-25T01:19:45Z |
| format | Article |
| id | doaj.art-dd5c6ffd103d4a67a15bd4ef3f3cf744 |
| institution | Directory Open Access Journal |
| issn | 2949-7744 |
| language | English |
| last_indexed | 2024-04-25T01:19:45Z |
| publishDate | 2024-01-01 |
| publisher | Elsevier |
| record_format | Article |
| series | Genetics in Medicine Open |
| spelling | doaj.art-dd5c6ffd103d4a67a15bd4ef3f3cf7442024-03-09T09:29:56ZengElsevierGenetics in Medicine Open2949-77442024-01-012100875O30: REKLAIM: A first in human phase Ib clinical trial of FBX-101 (AAVrh10.GALC) intravenously administered after UCBT for infantile Krabbe diseaseMaria Escolar0Mark Vander Lugt1Raymond Wang2Juan Ruiz3Michele Poe4Paul Szabolcs5Forge Biologics/University of PittsburghUniversity of MichiganChildren's Hospital of Orange CountyForge BiologicsForge BiologicsUniversity of Pittsburghhttp://www.sciencedirect.com/science/article/pii/S2949774424000219 |
| spellingShingle | Maria Escolar Mark Vander Lugt Raymond Wang Juan Ruiz Michele Poe Paul Szabolcs O30: REKLAIM: A first in human phase Ib clinical trial of FBX-101 (AAVrh10.GALC) intravenously administered after UCBT for infantile Krabbe disease Genetics in Medicine Open |
| title | O30: REKLAIM: A first in human phase Ib clinical trial of FBX-101 (AAVrh10.GALC) intravenously administered after UCBT for infantile Krabbe disease |
| title_full | O30: REKLAIM: A first in human phase Ib clinical trial of FBX-101 (AAVrh10.GALC) intravenously administered after UCBT for infantile Krabbe disease |
| title_fullStr | O30: REKLAIM: A first in human phase Ib clinical trial of FBX-101 (AAVrh10.GALC) intravenously administered after UCBT for infantile Krabbe disease |
| title_full_unstemmed | O30: REKLAIM: A first in human phase Ib clinical trial of FBX-101 (AAVrh10.GALC) intravenously administered after UCBT for infantile Krabbe disease |
| title_short | O30: REKLAIM: A first in human phase Ib clinical trial of FBX-101 (AAVrh10.GALC) intravenously administered after UCBT for infantile Krabbe disease |
| title_sort | o30 reklaim a first in human phase ib clinical trial of fbx 101 aavrh10 galc intravenously administered after ucbt for infantile krabbe disease |
| url | http://www.sciencedirect.com/science/article/pii/S2949774424000219 |
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