Respiratory morbidity in patients with spinal muscular atrophy—a changing world in the light of disease-modifying therapies

Respiratory morbidity in patients with spinal muscular atrophy—a changing world in the light of disease-modifying therapies

Respiratory complications are common in spinal muscular atrophy (SMA) and significantly contribute to morbidity and mortality in these patients. Generalized respiratory and bulbar muscle weakness translates into diverse and complex clinical consequences necessitating strict follow-up and specialized...

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Bibliographic Details
Main Authors: Leen Lagae, Marijke Proesmans, Marleen Van den Hauwe, François Vermeulen, Liesbeth De Waele, Mieke Boon
Format: Article
Language:English
Published: Frontiers Media S.A. 2024-03-01
Series:Frontiers in Pediatrics
Subjects:
spinal muscular atrophy
respiratory morbidity
disease-modifying therapies
nusinersen
onasemnogene abeparvovec
risdiplam
Online Access:https://www.frontiersin.org/articles/10.3389/fped.2024.1366943/full

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