In vivo treatment of tyrosinaemia with hypercompact Cas12f1

In vivo treatment of tyrosinaemia with hypercompact Cas12f1

Bibliographic Details
Main Authors:	Ruochen Guo, Zhifang Li, Guoling Li, Hainan Zhang, Chang Zhang, Xiaona Huo, Xiaoyin Zhang, Xiali Yang, Rongrong Yang, Yuanhua Liu, Xiaozhi Sun, Xinyu Liu, Hui Yang, Yingsi Zhou, Chunlong Xu
Format:	Article
Language:	English
Published:	Nature Publishing Group 2023-07-01
Series:	Cell Discovery
Online Access:	https://doi.org/10.1038/s41421-023-00554-y

Similar Items

Engineering a transposon-associated TnpB-ωRNA system for efficient gene editing and phenotypic correction of a tyrosinaemia mouse model
by: Zhifang Li, et al.
Published: (2024-01-01)

Molecular basis for DNA cleavage by the hypercompact Cas12j-SF05
by: Zhiqiang Duan, et al.
Published: (2023-11-01)

Recommendations for the management of tyrosinaemia type 1
by: de Laet Corinne, et al.
Published: (2013-01-01)

Hypercompact TnpB and truncated TnpB systems enable efficient genome editing in vitro and in vivo
by: Ming Wang, et al.
Published: (2024-03-01)

UK Dietary Practices for Tyrosinaemias: Time for Change
by: Anne Daly, et al.
Published: (2022-12-01)

Determinants of tyrosinaemia during nitisinone therapy in alkaptonuria
by: L. R. Ranganath, et al.
Published: (2022-09-01)

Diazoxide-responsive hyperinsulinaemic hypoglycaemia in tyrosinaemia type 1
by: Ellada Sotiridou, et al.
Published: (2021-01-01)

Modulation of metabolic functions through Cas13d-mediated gene knockdown in liver
by: Bingbing He, et al.
Published: (2020-03-01)

Develop a Compact RNA Base Editor by Fusing ADAR with Engineered EcCas6e
by: Xing Wang, et al.
Published: (2023-06-01)

Hepatorenal Tyrosinaemia: Impact of a Simplified Diet on Metabolic Control and Clinical Outcome
by: Friederike Bärhold, et al.
Published: (2020-12-01)

Natural Protein Tolerance and Metabolic Control in Patients with Hereditary Tyrosinaemia Type 1
by: Ozlem Yilmaz, et al.
Published: (2020-04-01)

Physical Growth of Patients with Hereditary Tyrosinaemia Type I: A Single-Centre Retrospective Study
by: Ozlem Yilmaz, et al.
Published: (2021-08-01)

Mini-dCas13X–mediated RNA editing restores dystrophin expression in a humanized mouse model of Duchenne muscular dystrophy
by: Guoling Li, et al.
Published: (2023-02-01)

Engineered CRISPR-OsCas12f1 and RhCas12f1 with robust activities and expanded target range for genome editing
by: Xiangfeng Kong, et al.
Published: (2023-04-01)

Small molecules enhance CRISPR/Cas9-mediated homology-directed genome editing in primary cells
by: Guoling Li, et al.
Published: (2017-08-01)

CRISPR/Cas9-Mediated Integration of Large Transgene into Pig CEP112 Locus
by: Guoling Li, et al.
Published: (2020-02-01)

Cas1 and Cas2 From the Type II-C CRISPR-Cas System of Riemerella anatipestifer Are Required for Spacer Acquisition
by: Yang He, et al.
Published: (2018-06-01)

Generation of Transgene-Free Semidwarf Maize Plants by Gene Editing of Gibberellin-Oxidase20-3 Using CRISPR/Cas9
by: Jiaojiao Zhang, et al.
Published: (2020-07-01)

Advances in application of CRISPR-Cas13a system
by: Yue Zhang, et al.
Published: (2024-02-01)

Expression of OsCAS (Calcium-Sensing Receptor) in an Arabidopsis Mutant Increases Drought Tolerance.
by: Xin Zhao, et al.
Published: (2015-01-01)

Generation of a homozygous CRISPR/Cas9-mediated knockout human iPSC line for PTCH1 gene
by: Bailing Zu, et al.
Published: (2021-10-01)

A Cas-embedding strategy for minimizing off-target effects of DNA base editors
by: Yajing Liu, et al.
Published: (2020-11-01)

Prevalence and related factors of first-time suicide attempts in the past 14 days in Chinese adult patients with first-episode drug-naïve major depressive disorder
by: Xiaoyin Cong, et al.
Published: (2024-03-01)

CRISPR/Cas9 technology and its application in horticultural crops
by: Yang Liu, et al.
Published: (2022-07-01)

Generation of Transgene-Free Maize Male Sterile Lines Using the CRISPR/Cas9 System
by: Rongrong Chen, et al.
Published: (2018-09-01)

Corrigendum to “Generation of a homozygous CRISPR/Cas9-mediated knockout human iPSC line for PTCH1 gene” [Stem Cell Res. 56 (2021) 102517]
by: Bailing Zu, et al.
Published: (2022-07-01)

Electrochemical Investigation of Chloride Ion-Induced Breakdown of Passive Film on P110 Casing Steel Surface in Simulated Pore Solution: Behavior and Critical Value Determination
by: Ye Peng, et al.
Published: (2024-01-01)

CRISPR–Cas9-mediated genomic multiloci integration in Pichia pastoris
by: Qi Liu, et al.
Published: (2019-08-01)

CRISPR/Cas9-mediated targeted chromosome elimination
by: Erwei Zuo, et al.
Published: (2017-11-01)

Electrical Conductivity of Eclogitic Omphacite and Garnet at Water-Rich Conditions
by: Hanyong Liu, et al.
Published: (2022-07-01)

Finite-Time Adaptive Fuzzy Consensus Stabilization for Unknown Nonlinear Leaderless Multi-Agent Systems With Unknown Output Dead-Zone
by: Hainan Yang, et al.
Published: (2019-01-01)

Youth and teenager health service in community organizing: prevention health care in China
by: Yang Wei, et al.
Published: (2019-07-01)

Treatment of autosomal dominant retinitis pigmentosa caused by RHO-P23H mutation with high-fidelity Cas13X in mice
by: Zixiang Yan, et al.
Published: (2023-09-01)

Relationship between Neuroticism and Gastrointestinal Symptoms in Irritable Bowel Syndrome: The Mediating Role of Sleep
by: Xiaoyin Cong, et al.
Published: (2022-09-01)

Multiple Bio-Inspired Father–Son Underwater Robot for Underwater Target Object Acquisition and Identification
by: Ruochen An, et al.
Published: (2021-12-01)

A Novel Process Monitoring Method Based on Dynamic Related ReliefF-SFA Method
by: Xiaozhi Liu, et al.
Published: (2020-01-01)

CRISPR/Cas9 therapeutics: progress and prospects
by: Tianxiang Li, et al.
Published: (2023-01-01)

CRISPR-CasRx Targeting LncRNA LINC00341 Inhibits Tumor Cell Growth in vitro and in vivo
by: Chunjing Li, et al.
Published: (2021-03-01)

Optimization of CRISPR-Cas9 system in Eustoma grandiflorum
by: Xueqi Li, et al.
Published: (2024-03-01)

Establishment of Agrobacterium-mediated genetic transformation and application of CRISPR/Cas9 genome-editing system to Brassica rapa var. rapa
by: Yuanyuan Liu, et al.
Published: (2022-08-01)