Editorial: Ex-vivo and in-vivo genome engineering for metabolic and neurometabolic diseases

Bibliographic Details
Main Authors: Pasqualina Colella, Vasco Meneghini, Guilherme Baldo, Natalia Gomez-Ospina
Format: Article
Language:English
Published: Frontiers Media S.A. 2023-07-01
Series:Frontiers in Genome Editing
Subjects:
Online Access:https://www.frontiersin.org/articles/10.3389/fgeed.2023.1248904/full
_version_ 1797785616651386880
author Pasqualina Colella
Vasco Meneghini
Vasco Meneghini
Guilherme Baldo
Natalia Gomez-Ospina
author_facet Pasqualina Colella
Vasco Meneghini
Vasco Meneghini
Guilherme Baldo
Natalia Gomez-Ospina
author_sort Pasqualina Colella
collection DOAJ
first_indexed 2024-03-13T00:57:35Z
format Article
id doaj.art-e86efa01aac249639a95a8183942dc2a
institution Directory Open Access Journal
issn 2673-3439
language English
last_indexed 2024-03-13T00:57:35Z
publishDate 2023-07-01
publisher Frontiers Media S.A.
record_format Article
series Frontiers in Genome Editing
spelling doaj.art-e86efa01aac249639a95a8183942dc2a2023-07-06T18:45:59ZengFrontiers Media S.A.Frontiers in Genome Editing2673-34392023-07-01510.3389/fgeed.2023.12489041248904Editorial: Ex-vivo and in-vivo genome engineering for metabolic and neurometabolic diseasesPasqualina Colella0Vasco Meneghini1Vasco Meneghini2Guilherme Baldo3Natalia Gomez-Ospina4Department of Pediatrics, Stanford University, Stanford, CA, United StatesSan Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute, Milan, ItalyVita-Salute San Raffaele University, Milan, ItalyClinical Hospital of Porto Alegre, Federal University of Rio Grande do Sul, Porto Alegre, BrazilDepartment of Pediatrics, Stanford University, Stanford, CA, United Stateshttps://www.frontiersin.org/articles/10.3389/fgeed.2023.1248904/fullgenome editingneurometabolicliverretinaHSPCmetabolic
spellingShingle Pasqualina Colella
Vasco Meneghini
Vasco Meneghini
Guilherme Baldo
Natalia Gomez-Ospina
Editorial: Ex-vivo and in-vivo genome engineering for metabolic and neurometabolic diseases
Frontiers in Genome Editing
genome editing
neurometabolic
liver
retina
HSPC
metabolic
title Editorial: Ex-vivo and in-vivo genome engineering for metabolic and neurometabolic diseases
title_full Editorial: Ex-vivo and in-vivo genome engineering for metabolic and neurometabolic diseases
title_fullStr Editorial: Ex-vivo and in-vivo genome engineering for metabolic and neurometabolic diseases
title_full_unstemmed Editorial: Ex-vivo and in-vivo genome engineering for metabolic and neurometabolic diseases
title_short Editorial: Ex-vivo and in-vivo genome engineering for metabolic and neurometabolic diseases
title_sort editorial ex vivo and in vivo genome engineering for metabolic and neurometabolic diseases
topic genome editing
neurometabolic
liver
retina
HSPC
metabolic
url https://www.frontiersin.org/articles/10.3389/fgeed.2023.1248904/full
work_keys_str_mv AT pasqualinacolella editorialexvivoandinvivogenomeengineeringformetabolicandneurometabolicdiseases
AT vascomeneghini editorialexvivoandinvivogenomeengineeringformetabolicandneurometabolicdiseases
AT vascomeneghini editorialexvivoandinvivogenomeengineeringformetabolicandneurometabolicdiseases
AT guilhermebaldo editorialexvivoandinvivogenomeengineeringformetabolicandneurometabolicdiseases
AT nataliagomezospina editorialexvivoandinvivogenomeengineeringformetabolicandneurometabolicdiseases