Disease progression modeling of the North Star Ambulatory Assessment for Duchenne Muscular Dystrophy

Disease progression modeling of the North Star Ambulatory Assessment for Duchenne Muscular Dystrophy

Abstract Duchenne muscular dystrophy (DMD) is a rare genetic disorder caused by decreased or absent dystrophin gene leading to progressive muscle degeneration and weakness in young boys. Disease progression models for the North Star Ambulatory Assessment (NSAA), a functional measurement widely used...

Full description

Bibliographic Details
Main Authors: Jennifer E. Hibma, Priya Jayachandran, Srividya Neelakantan, Lutz O. Harnisch
Format: Article
Language:English
Published: Wiley 2023-03-01
Series:CPT: Pharmacometrics & Systems Pharmacology
Online Access:https://doi.org/10.1002/psp4.12921

Similar Items

Similar Items