S272: SAFETY AND EFFICACY OF RM-001 IN PATIENTS WITH TRANSFUSION-DEPENDENT Β-THALASSEMIA: EARLY RESULTS FROM THE ONGOING OF AUTOLOGOUS HBG1/2 PROMOTER-MODIFIED CD34+ HEMATOPOIETIC STEM AND PROGENITOR CELLS
| Main Authors: | , , , , , , , , , , , , , , , , , , |
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| Format: | Article |
| Language: | English |
| Published: |
Wiley
2023-08-01
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| Series: | HemaSphere |
| Online Access: | http://journals.lww.com/10.1097/01.HS9.0000968000.61396.5e |
| _version_ | 1827331229182066688 |
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| author | Rongrong Liu LI Wang Hui Xu Xiaolin Yin Junbin Liang Wenqiang Xie Gaohui Yang Yaoyun LI Yali Zhou Lei Shi Bin Xiao Lingling Shi Zeyan Shi Xuemei Zhou Jianpei Fang Xiangmin Xu Yongrong Lai Junjiu Huang Xinhua Zhang |
| author_facet | Rongrong Liu LI Wang Hui Xu Xiaolin Yin Junbin Liang Wenqiang Xie Gaohui Yang Yaoyun LI Yali Zhou Lei Shi Bin Xiao Lingling Shi Zeyan Shi Xuemei Zhou Jianpei Fang Xiangmin Xu Yongrong Lai Junjiu Huang Xinhua Zhang |
| author_sort | Rongrong Liu |
| collection | DOAJ |
| first_indexed | 2024-03-07T16:33:04Z |
| format | Article |
| id | doaj.art-f2d882b7e50740e98d339817b41d225d |
| institution | Directory Open Access Journal |
| issn | 2572-9241 |
| language | English |
| last_indexed | 2024-03-07T16:33:04Z |
| publishDate | 2023-08-01 |
| publisher | Wiley |
| record_format | Article |
| series | HemaSphere |
| spelling | doaj.art-f2d882b7e50740e98d339817b41d225d2024-03-03T10:10:27ZengWileyHemaSphere2572-92412023-08-017e613965e10.1097/01.HS9.0000968000.61396.5e202308003-00174S272: SAFETY AND EFFICACY OF RM-001 IN PATIENTS WITH TRANSFUSION-DEPENDENT Β-THALASSEMIA: EARLY RESULTS FROM THE ONGOING OF AUTOLOGOUS HBG1/2 PROMOTER-MODIFIED CD34+ HEMATOPOIETIC STEM AND PROGENITOR CELLSRongrong Liu0LI Wang1Hui Xu2Xiaolin Yin3Junbin Liang4Wenqiang Xie5Gaohui Yang6Yaoyun LI7Yali Zhou8Lei Shi9Bin Xiao10Lingling Shi11Zeyan Shi12Xuemei Zhou13Jianpei Fang14Xiangmin Xu15Yongrong Lai16Junjiu Huang17Xinhua Zhang181 The First Affiliated Hospital of Guangxi Medical University, Hematology, Nanning, China2 923rd Hospital of the People’s Liberation Army, Pediatric, Nanning, China3 Reforgene Medicine, Guangzhou, China4 923rd Hospital of the People’s Liberation Army, Hematology, Nanning, China3 Reforgene Medicine, Guangzhou, China1 The First Affiliated Hospital of Guangxi Medical University, Hematology, Nanning, China1 The First Affiliated Hospital of Guangxi Medical University, Hematology, Nanning, China2 923rd Hospital of the People’s Liberation Army, Pediatric, Nanning, China4 923rd Hospital of the People’s Liberation Army, Hematology, Nanning, China3 Reforgene Medicine, Guangzhou, China2 923rd Hospital of the People’s Liberation Army, Pediatric, Nanning, China1 The First Affiliated Hospital of Guangxi Medical University, Hematology, Nanning, China1 The First Affiliated Hospital of Guangxi Medical University, Hematology, Nanning, China1 The First Affiliated Hospital of Guangxi Medical University, Hematology, Nanning, China5 Sun Yat-Sen Memorial Hospital of Sun Yat-Sen University, Pediatric, Guangzhou, China6 School of Basic Medical Sciences, Southern Medical University, Medical Genetics, Guangzhou, China1 The First Affiliated Hospital of Guangxi Medical University, Hematology, Nanning, China7 School of Life Sciences, Sun Yat-Sen University, Guangzhou, China4 923rd Hospital of the People’s Liberation Army, Hematology, Nanning, Chinahttp://journals.lww.com/10.1097/01.HS9.0000968000.61396.5e |
| spellingShingle | Rongrong Liu LI Wang Hui Xu Xiaolin Yin Junbin Liang Wenqiang Xie Gaohui Yang Yaoyun LI Yali Zhou Lei Shi Bin Xiao Lingling Shi Zeyan Shi Xuemei Zhou Jianpei Fang Xiangmin Xu Yongrong Lai Junjiu Huang Xinhua Zhang S272: SAFETY AND EFFICACY OF RM-001 IN PATIENTS WITH TRANSFUSION-DEPENDENT Β-THALASSEMIA: EARLY RESULTS FROM THE ONGOING OF AUTOLOGOUS HBG1/2 PROMOTER-MODIFIED CD34+ HEMATOPOIETIC STEM AND PROGENITOR CELLS HemaSphere |
| title | S272: SAFETY AND EFFICACY OF RM-001 IN PATIENTS WITH TRANSFUSION-DEPENDENT Β-THALASSEMIA: EARLY RESULTS FROM THE ONGOING OF AUTOLOGOUS HBG1/2 PROMOTER-MODIFIED CD34+ HEMATOPOIETIC STEM AND PROGENITOR CELLS |
| title_full | S272: SAFETY AND EFFICACY OF RM-001 IN PATIENTS WITH TRANSFUSION-DEPENDENT Β-THALASSEMIA: EARLY RESULTS FROM THE ONGOING OF AUTOLOGOUS HBG1/2 PROMOTER-MODIFIED CD34+ HEMATOPOIETIC STEM AND PROGENITOR CELLS |
| title_fullStr | S272: SAFETY AND EFFICACY OF RM-001 IN PATIENTS WITH TRANSFUSION-DEPENDENT Β-THALASSEMIA: EARLY RESULTS FROM THE ONGOING OF AUTOLOGOUS HBG1/2 PROMOTER-MODIFIED CD34+ HEMATOPOIETIC STEM AND PROGENITOR CELLS |
| title_full_unstemmed | S272: SAFETY AND EFFICACY OF RM-001 IN PATIENTS WITH TRANSFUSION-DEPENDENT Β-THALASSEMIA: EARLY RESULTS FROM THE ONGOING OF AUTOLOGOUS HBG1/2 PROMOTER-MODIFIED CD34+ HEMATOPOIETIC STEM AND PROGENITOR CELLS |
| title_short | S272: SAFETY AND EFFICACY OF RM-001 IN PATIENTS WITH TRANSFUSION-DEPENDENT Β-THALASSEMIA: EARLY RESULTS FROM THE ONGOING OF AUTOLOGOUS HBG1/2 PROMOTER-MODIFIED CD34+ HEMATOPOIETIC STEM AND PROGENITOR CELLS |
| title_sort | s272 safety and efficacy of rm 001 in patients with transfusion dependent β thalassemia early results from the ongoing of autologous hbg1 2 promoter modified cd34 hematopoietic stem and progenitor cells |
| url | http://journals.lww.com/10.1097/01.HS9.0000968000.61396.5e |
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