Deriving Vignettes for the Rare Disease AADC Deficiency Using Parent, Caregiver and Clinician Interviews to Evaluate the Impact on Health-Related Quality of Life
Andria Hanbury,1 Adam B Smith,1 Katharina Buesch2 1York Health Economics Consortium, University of York, York YO10 5NQ, UK; 2PTC Therapeutics, Zug 6300, SwitzerlandCorrespondence: Adam B SmithYork Health Economics Consortium, Enterprise House, Innovation Way, University of York, York YO10 5NQ, UKTel...
Main Authors: | Hanbury A, Smith AB, Buesch K |
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Format: | Article |
Language: | English |
Published: |
Dove Medical Press
2021-01-01
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Series: | Patient Related Outcome Measures |
Subjects: | |
Online Access: | https://www.dovepress.com/deriving-vignettes-for-the-rare-disease-aadc-deficiency-using-parent-c-peer-reviewed-article-PROM |
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