Hutchinson-Gilford Progeria Syndrome—Current Status and Prospects for Gene Therapy Treatment

Hutchinson-Gilford Progeria Syndrome—Current Status and Prospects for Gene Therapy Treatment

Hutchinson-Gilford progeria syndrome (HGPS) is one of the most severe disorders among laminopathies&#8212;a heterogeneous group of genetic diseases with a molecular background based on mutations in the <i>LMNA</i> gene and genes coding for interacting proteins. HGPS is characterized...

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Bibliographic Details
Main Authors: Katarzyna Piekarowicz, Magdalena Machowska, Volha Dzianisava, Ryszard Rzepecki
Format: Article
Language:English
Published: MDPI AG 2019-01-01
Series:Cells
Subjects:
HGPS
laminopathy
lamin A/C
progerin
gene therapy
miR9
Online Access:https://www.mdpi.com/2073-4409/8/2/88

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