Spinal muscular atrophy: a perspective outlook
Background. Recent decades have witnessed a leap in understanding the molecular genetic bases of spinal muscular atrophy for a considerable improvement in diagnosis and treatment of this disease and development of innovative therapies for correcting genetic deficiencies. Given scarcity of etiotropic...
Main Authors: | M. R. Shaimurzin, I. S. Lutskiy |
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Format: | Article |
Language: | Russian |
Published: |
Ministry of Healthcare of the Russian Federation. “Kuban State Medical University”
2020-12-01
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Series: | Кубанский научный медицинский вестник |
Subjects: | |
Online Access: | https://ksma.elpub.ru/jour/article/view/2288 |
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