Cost-effectiveness of voretigene neparvovec in the treatment of patients with inherited retinal disease with RPE65 mutation in Switzerland
Abstract Objective We aimed to evaluate the cost-effectiveness of voretigene neparvovec (VN) compared with standard of care (SoC) for patients with inherited retinal disease (IRD) caused by a biallelic RPE65-mutation. VN is a live, non-replicating adeno-associated virus serotype 2 (AAV2). SoC is bes...
Main Authors: | Arjun Bhadhuri, Daniel Dröschel, Mike Guldimann, Claudia Jetschgo, Judit Banhazi, Matthias Schwenkglenks, C. Simone Sutherland |
---|---|
Format: | Article |
Language: | English |
Published: |
BMC
2022-06-01
|
Series: | BMC Health Services Research |
Subjects: | |
Online Access: | https://doi.org/10.1186/s12913-022-08211-y |
Similar Items
-
RPE65-associated inherited retinal diseases: consensus recommendations for eligibility to gene therapy
by: Andrea Sodi, et al.
Published: (2021-06-01) -
Outcomes and Adverse Effects of Voretigene Neparvovec Treatment for Biallelic <i>RPE65</i>-Mediated Inherited Retinal Dystrophies in a Cohort of Patients from a Single Center
by: Peter Kiraly, et al.
Published: (2023-10-01) -
Voretigene Neparvovec in Retinal Diseases: A Review of the Current Clinical Evidence
by: Gao J, et al.
Published: (2020-11-01) -
Voretigene Neparvovec and Gene Therapy for Leber’s Congenital Amaurosis: Review of Evidence to Date
by: Padhy SK, et al.
Published: (2020-11-01) -
Real-World Safety and Effectiveness of Voretigene Neparvovec: Results up to 2 Years from the Prospective, Registry-Based PERCEIVE Study
by: M. Dominik Fischer, et al.
Published: (2024-01-01)