Multiplex precise base editing in cynomolgus monkeys

© 2020, The Author(s). Common polygenic diseases result from compounded risk contributed by multiple genetic variants, meaning that simultaneous correction or introduction of single nucleotide variants is required for disease modeling and gene therapy. Here, we show precise, efficient, and simultane...

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Main Authors: Zhang, Wenhui, Aida, Tomomi, del Rosario, Ricardo CH, Wilde, Jonathan J, Ding, Chenhui, Zhang, Xiaohui, Baloch, Zulqurain, Huang, Yan, Tang, Yu, Li, Duanduan, Lu, Hongyu, Zhou, Yang, Jiang, Minqing, Xu, Dongdong, Fang, Zhihao, Zheng, Zhanhong, Huang, Qunshan, Feng, Guoping, Yang, Shihua
其他作者: McGovern Institute for Brain Research at MIT
格式: 文件
语言:English
出版: Springer Science and Business Media LLC 2021
在线阅读:https://hdl.handle.net/1721.1/133744

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