IGF1 as a Potential Treatment for Rett Syndrome: Safety Assessment in Six Rett Patients

IGF1 as a Potential Treatment for Rett Syndrome: Safety Assessment in Six Rett Patients

Rett syndrome (RTT) is a devastating neurodevelopmental disorder that affects one in ten thousand girls and has no cure. The majority of RTT patients display mutations in the gene that codes for the methyl-CpG-binding protein 2 (MeCP2). Clinical observations and neurobiological analysis of mouse mod...

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Bibliographic Details
Main Authors: Pini, Giorgio, Scusa, Maria Flora, Congiu, Laura, Benincasa, Alberto, Morescalchi, Paolina, Bottiglioni, Ilaria, Di Marco, Pietro, Borelli, Paolo, Bonuccelli, Ubaldo, Della-Chiesa, Andrea, Prina-Mello, Adriele, Tropea, Daniela
Other Authors: Massachusetts Institute of Technology. Department of Brain and Cognitive Sciences
Format: Article
Language:English
Published: Hindawi Publishing Corporation 2015
Online Access:http://hdl.handle.net/1721.1/96244
https://orcid.org/0000-0001-9730-6636

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