Emerging oligonucleotide therapeutics for rare neuromuscular diseases
Research and drug development concerning rare diseases are at the cutting edge of scientific technology. To date, over 7,000 rare diseases have been identified. Despite their individual rarity, 1 in 10 individuals worldwide is affected by a rare condition. For the majority of these diseases, there i...
Main Authors: | Aoki, Y, Wood, MJA |
---|---|
פורמט: | Journal article |
שפה: | English |
יצא לאור: |
IOS Press
2021
|
פריטים דומים
-
Oligonucleotide-based therapies for neuromuscular disease
מאת: Douglas, A, et al.
יצא לאור: (2015) -
Peptide-conjugate antisense based splice-correction for Duchenne muscular dystrophy and other neuromuscular diseases
מאת: Tsoumpra, MK, et al.
יצא לאור: (2019) -
Advances in oligonucleotide drug delivery
מאת: Roberts, TC, et al.
יצא לאור: (2020) -
Recent advances in antisense oligonucleotide therapy in genetic neuromuscular diseases
מאת: Ashok Verma
יצא לאור: (2018-01-01) -
Cell-penetrating peptide conjugates of steric blocking oligonucleotides as therapeutics for neuromuscular diseases from a historical perspective to current prospects of treatment
מאת: Gait, M, et al.
יצא לאור: (2018)