Emerging oligonucleotide therapeutics for rare neuromuscular diseases

Research and drug development concerning rare diseases are at the cutting edge of scientific technology. To date, over 7,000 rare diseases have been identified. Despite their individual rarity, 1 in 10 individuals worldwide is affected by a rare condition. For the majority of these diseases, there i...

Descripció completa

Dades bibliogràfiques
Autors principals: Aoki, Y, Wood, MJA
Format: Journal article
Idioma:English
Publicat: IOS Press 2021