Gene therapy for surfactant protein B deficiency using recombinant AAV vectors

Gene therapies are being developed for rare genetic diseases and offer hope for conditions with few treatment options. Surfactant protein B (SP-B) deficiency is a rare genetic disease of the lung causing severe respiratory distress in neonates and is fatal within the first months of life. Recombinan...

Cur síos iomlán

Sonraí bibleagrafaíochta
Príomhchruthaitheoir: Meyer-Berg, H
Rannpháirtithe: Gill, D
Formáid: Tráchtas
Teanga:English
Foilsithe / Cruthaithe: 2021
Ábhair: