Preclinical studies of WVE-210201, an investigational stereopure antisense oligonucleotide in development for the treatment of patients with duchenne muscular dystrophy (DMD)

Eitemau Tebyg

• Advancing the potential of peptide-PMO compounds in exon skipping therapy for DMD
  gan: Godfrey, C, et al.
  Cyhoeddwyd: (2012)
• Complete cloning of the Duchenne muscular dystrophy (DMD) cDNA and preliminary genomic organization of the DMD gene in normal and affected individuals.
  gan: Koenig, M, et al.
  Cyhoeddwyd: (1987)
• Clinical trials using antisense oligonucleotides in duchenne muscular dystrophy.
  gan: Koo, T, et al.
  Cyhoeddwyd: (2013)
• PRO-051, an antisense oligonucleotide for the potential treatment of Duchenne muscular dystrophy.
  gan: Hammond, S, et al.
  Cyhoeddwyd: (2010)
• Preclinical development of antisense conjugates for the treatment of myotonic dystrophy 1
  gan: Stoodley, J
  Cyhoeddwyd: (2024)