Spatial and subcellular gene expression patterns in myogenic differentiation and muscle pathology
<p>Duchenne muscular dystrophy (DMD) is a debilitating muscle-wasting disorder caused by lack of dystrophin protein. Promising dystrophin-restoration therapies such as gene editing using the CRISPR-Cas9 system and antisense oligonucleotide-mediated exon skipping using peptide-phosphorodiamidat...
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| Format: | Thesis |
| Language: | English |
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2024
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