SAFETY AND EXPRESSION OF A SINGLE DOSE OF LIPID-MEDIATED CFTR GENE THERAPY TO THE UPPER AND LOWER AIRWAYS OF PATIENTS WITH CYSTIC FIBROSIS

SAFETY AND EXPRESSION OF A SINGLE DOSE OF LIPID-MEDIATED CFTR GENE THERAPY TO THE UPPER AND LOWER AIRWAYS OF PATIENTS WITH CYSTIC FIBROSIS

Manylion Llyfryddiaeth
Prif Awduron:	Davies, G, Davies, J, Gill, DR, Hyde, S, Boyd, C, Innes, J, Porteous, D, Cheng, S, Scheule, R, Higgins, T, Griesenbach, U, Alton, E
Fformat:	Conference item
Cyhoeddwyd:	2011

Eitemau Tebyg

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A randomised, double-blind, placebo-controlled phase IIB clinical trial of repeated application of gene therapy in patients with cystic fibrosis
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Self-reactive CFTR T cells in humans: implications for gene therapy.
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UPDATE ON THE UK CF GENE THERAPY CONSORTIUM MULTIDOSE, NON-VIRAL, GENE THERAPY TRIAL
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