SAFETY AND EXPRESSION OF A SINGLE DOSE OF LIPID-MEDIATED CFTR GENE THERAPY TO THE UPPER AND LOWER AIRWAYS OF PATIENTS WITH CYSTIC FIBROSIS
Prif Awduron: | Davies, G, Davies, J, Gill, DR, Hyde, S, Boyd, C, Innes, J, Porteous, D, Cheng, S, Scheule, R, Higgins, T, Griesenbach, U, Alton, E |
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Fformat: | Conference item |
Cyhoeddwyd: |
2011
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Eitemau Tebyg
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SAFETY AND EXPRESSION OF A SINGLE DOSE OF LIPID-MEDIATED CFTR GENE THERAPY TO THE UPPER AND LOWER AIRWAYS OF PATIENTS WITH CF
gan: Davies, J, et al.
Cyhoeddwyd: (2011) -
A randomised, double-blind, placebo-controlled phase IIB clinical trial of repeated application of gene therapy in patients with cystic fibrosis
gan: Alton, E, et al.
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A randomised, double-blind, placebo-controlled phase IIB clinical trial of repeated application of gene therapy in patients with cystic fibrosis.
gan: Alton, E, et al.
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A randomized, double-blind, placebo-controlled trial of repeated nebulisation of non-viral CFTR gene therapy in patients with cystic fibrosis
gan: Alton, E, et al.
Cyhoeddwyd: (2015) -
EVALUATION OF SAFETY AND GENE EXPRESSION WITH A SINGLE DOSE OF PGM169/GL67A ADMINISTERED TO THE NOSE AND LUNG OF INDIVIDUALS WITH CYSTIC FIBROSIS: THE UK CF GENE THERAPY CONSORTIUM "PILOT STUDY''
gan: Davies, J, et al.
Cyhoeddwyd: (2009)