SAFETY AND EXPRESSION OF A SINGLE DOSE OF LIPID-MEDIATED CFTR GENE THERAPY TO THE UPPER AND LOWER AIRWAYS OF PATIENTS WITH CYSTIC FIBROSIS

SAFETY AND EXPRESSION OF A SINGLE DOSE OF LIPID-MEDIATED CFTR GENE THERAPY TO THE UPPER AND LOWER AIRWAYS OF PATIENTS WITH CYSTIC FIBROSIS

书目详细资料
Main Authors:	Davies, G, Davies, J, Gill, DR, Hyde, S, Boyd, C, Innes, J, Porteous, D, Cheng, S, Scheule, R, Higgins, T, Griesenbach, U, Alton, E
格式:	Conference item
出版:	2011

相似书籍

SAFETY AND EXPRESSION OF A SINGLE DOSE OF LIPID-MEDIATED CFTR GENE THERAPY TO THE UPPER AND LOWER AIRWAYS OF PATIENTS WITH CF
由: Davies, J, et al.
出版: (2011)

A randomised, double-blind, placebo-controlled phase IIB clinical trial of repeated application of gene therapy in patients with cystic fibrosis
由: Alton, E, et al.
出版: (2013)

A randomised, double-blind, placebo-controlled phase IIB clinical trial of repeated application of gene therapy in patients with cystic fibrosis.
由: Alton, E, et al.
出版: (2013)

A randomized, double-blind, placebo-controlled trial of repeated nebulisation of non-viral CFTR gene therapy in patients with cystic fibrosis
由: Alton, E, et al.
出版: (2015)

EVALUATION OF SAFETY AND GENE EXPRESSION WITH A SINGLE DOSE OF PGM169/GL67A ADMINISTERED TO THE NOSE AND LUNG OF INDIVIDUALS WITH CYSTIC FIBROSIS: THE UK CF GENE THERAPY CONSORTIUM "PILOT STUDY''
由: Davies, J, et al.
出版: (2009)

Self-reactive CFTR T cells in humans: implications for gene therapy.
由: Calcedo, R, et al.
出版: (2013)

Cumulative CFTR expression following repeated aerosol delivery of non-viral pGM169/GL67A formulation to mouse lung
由: Alton, E, et al.
出版: (2012)

REPEAT ADMINISTRATION OF GL67A/PGM169 IS FEASIBLE, SAFE, AND PRODUCES ENDOGENOUS LEVELS OF CFTR EXPRESSION AFTER 12 DOSES
由: Alton, E, et al.
出版: (2012)

A PHASE 2B DOUBLE-BLIND, PLACEBO-CONTROLLED TRIAL OF NON-VIRAL MEDIATED GENE THERAPY FOR CF
由: Alton, E, et al.
出版: (2013)

Low levels of CFTR gene transfer with F/HN pseudotyped lentivirus are sufficient to generate ion transport correction in airway cell cultures from cystic fibrosis patients
由: Sergijenko, A, et al.
出版: (2020)

Toxicology study assessing efficacy and safety of repeated administration of lipid/DNA complexes to mouse lung.
由: Alton, E, et al.
出版: (2014)

Toxicology study assessing efficacy and safety of repeated administration of lipid/DNA complexes to mouse lung
由: Alton, E, et al.
出版: (2014)

The safety profile of a cationic lipid-mediated cystic fibrosis gene transfer agent following repeated monthly aerosol administration to sheep
由: Alton, E, et al.
出版: (2013)

The safety profile of a cationic lipid-mediated cystic fibrosis gene transfer agent following repeated monthly aerosol administration to sheep.
由: Alton, E, et al.
出版: (2013)

Preparation for a first-in-man lentivirus trial in cystic fibrosis patients
由: Griesenbach, U, et al.
出版: (2016)

Assessment of CFTR function after gene transfer in vitro and in vivo.
由: Griesenbach, U, et al.
出版: (2008)

EVALUATION OF SAFETY AND GENE EXPRESSION WITH A SINGLE DOSE OF PGM169/GL67A ADMINISTERED TO THE NOSE AND LUNG OF INDIVIDUALS WITH CF: THE UK CF GENE THERAPY CONSORTIUM "PILOT STUDY"
由: Davies, J, et al.
出版: (2009)

CFTR dysfunction leads to defective bacterial eradication on cystic fibrosis airways
由: Min Wu, et al.
出版: (2024-04-01)

CFTR Modulator Therapies: Potential Impact on Airway Infections in Cystic Fibrosis
由: Francesca Saluzzo, et al.
出版: (2022-04-01)

Changes in the Cystic Fibrosis Airway Microbiome in Response to CFTR Modulator Therapy
由: Buqing Yi, et al.
出版: (2021-03-01)

TOXICOLOGY STUDIES IN SUPPORT OF THE UK CF GENE THERAPY CONSORTIUM'S MULTI-DOSE CLINICAL TRIAL
由: Griesenbach, U, et al.
出版: (2011)

Non-viral CFTR gene delivery to the lungs of Cystic Fibrosis patients
由: Hyde, S
出版: (2013)

Detection of CFTR transgene mRNA expression in respiratory epithelium isolated from the murine nasal cavity.
由: Holder, E, et al.
出版: (2010)

LONGITUDINAL ASSESSMENT OF BIOMARKERS FOR CLINICAL TRIALS OF NOVEL THERAPEUTIC AGENTS; THE RUN-IN STUDY
由: Alton, E, et al.
出版: (2010)

Sendai virus-mediated CFTR gene transfer to the airway epithelium.
由: Ferrari, S, et al.
出版: (2007)

A randomised, double-blind, placebo-controlled trial of repeated nebulisation of non-viral cystic fibrosis transmembrane conductance regulator (CFTR) gene therapy in patients with cystic fibrosis
由: Alton, EWFW, et al.
出版: (2016)

UPDATE ON THE UK CF GENE THERAPY CONSORTIUM MULTIDOSE, NON-VIRAL, GENE THERAPY TRIAL
由: Alton, E, et al.
出版: (2012)

UPDATE ON THE UK CF GENE THERAPY CONSORTIUM MULTIDOSE, NON-VIRAL, GENE THERAPY TRIAL
由: Alton, E, et al.
出版: (2012)

CFTR targeted therapies: recent advances in cystic fibrosis and possibilities in other diseases of the airways
由: Sheylan D. Patel, et al.
出版: (2020-06-01)

Cystic fibrosis transmembrane conductance regulator (CFTR): beyond cystic fibrosis
由: Giuseppe Fabio Parisi, et al.
出版: (2022-05-01)

Exploring the mechanisms of macrolides in cystic fibrosis.
由: Equi, A, et al.
出版: (2006)

LONGITUDINAL ASSESSMENT OF BIOMARKERS FOR CLINICAL TRIALS OF NOVEL THERAPEUTIC AGENTS: THE RUN-IN STUDY
由: Alton, E, et al.
出版: (2010)

Cystic fibrosis transmembrane conductance regulator (CFTR)-targeted therapeutics for cystic fibrosis
由: Veselu, D-F, et al.
出版: (2024)

Cystic Fibrosis and Oxidative Stress: The Role of CFTR
由: Evelina Moliteo, et al.
出版: (2022-08-01)

The Cystic Fibrosis Transmembrane Regulator (CFTR) in the kidney
由: MARCELO M. MORALES, et al.
出版: (2000-09-01)

CFTR and Ca2+ signaling in cystic fibrosis
由: Fabrice eAntigny, et al.
出版: (2011-10-01)

Strategies to circumvent the CFTR defect in cystic fibrosis
由: Frederic eBecq, et al.
出版: (2013-08-01)

Not All Is CFTR – Neutrophils and Cholesterol in Cystic Fibrosis
由: Stefano Castellani, et al.
出版: (2017-10-01)

A randomised, double-blind, placebo-controlled trial of repeated nebulisation of non-viral cystic fibrosis transmembrane conductance regulator (CFTR) gene therapy in patients with cystic fibrosis
由: Eric WFW Alton, et al.
出版: (2016-07-01)

The cystic fibrosis lower airways microbial metagenome
由: Patricia Moran Losada, et al.
出版: (2016-05-01)