Therapy for Duchenne muscular dystrophy: renewed optimism from genetic approaches.
Duchenne muscular dystrophy (DMD) is a devastating progressive disease for which there is currently no effective treatment except palliative therapy. There are several promising genetic approaches, including viral delivery of the missing dystrophin gene, read-through of translation stop codons, exon...
| Main Authors: | , , |
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| Format: | Journal article |
| Language: | English |
| Published: |
2013
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