Development of CRISPR gene therapy for retinal degenerations
<p>Inherited retinal degenerations (IRDs) are a leading cause of blindness, caused by mutations in genes leading to dysfunction and death of cells in the outer retina. Gene-supplementation therapies using adeno-associated viral (AAV) vectors have been developed, however, they are limited to th...
| Autor principal: | |
|---|---|
| Outros Autores: | |
| Formato: | Tese |
| Idioma: | English |
| Publicado em: |
2021
|
| Assuntos: |