Development of CRISPR-Cas genome and epigenome engineering tools towards retinal degenerations
<p>Inherited retinal diseases (IRDs) are a diverse family of disorders caused by genetic mutations that lead to dysfunction and death of cells in the outer retina. Together, they are the most common cause of untreatable blindness in the working age population. While gene supplementation therap...
| Autor principal: | |
|---|---|
| Outros Autores: | |
| Formato: | Thesis |
| Idioma: | English |
| Publicado em: |
2022
|
| Assuntos: |