Gene therapy for surfactant protein B deficiency using recombinant AAV

Gene therapy for surfactant protein B deficiency using recombinant AAV

Manylion Llyfryddiaeth
Prif Awduron:	Meyer-Berg, H, Hyde, S, Gill, D
Fformat:	Conference item
Cyhoeddwyd:	Elsevier 2019

Eitemau Tebyg

Gene therapy for surfactant protein B deficiency using recombinant AAV vectors
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Immunogenicity and toxicity of AAV gene therapy
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Corrigendum: Optimized riboswitch-regulated AAV vector for VEGF-B gene therapy
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Inclusion of PF68 surfactant improves stability of rAAV titer when passed through a surgical device used in retinal gene therapy
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Rational Design of AAV-rh74, AAV3B, and AAV8 with Limited Liver Targeting
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Optimizing an AAV-CRISPR system for retinal gene therapy
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Choroideremia: molecular mechanisms and development of AAV gene therapy
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Immunogenicity of Novel AAV Capsids for Retinal Gene Therapy
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Emerging Issues in AAV-Mediated In Vivo Gene Therapy
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