Gene therapy for surfactant protein B deficiency using recombinant AAV

Gene therapy for surfactant protein B deficiency using recombinant AAV

Λεπτομέρειες βιβλιογραφικής εγγραφής
Κύριοι συγγραφείς:	Meyer-Berg, H, Hyde, S, Gill, D
Μορφή:	Conference item
Έκδοση:	Elsevier 2019

Παρόμοια τεκμήρια

Gene therapy for surfactant protein B deficiency using recombinant AAV vectors
ανά: Meyer-Berg, H
Έκδοση: (2021)

A human surfactant B deficiency air-liquid interface cell culture model suitable for gene therapy applications
ανά: Munis, AM, κ.ά.
Έκδοση: (2020)

A human surfactant B deficiency air-liquid interface cell culture model suitable for gene therapy applications
ανά: Altar M. Munis, κ.ά.
Έκδοση: (2021-03-01)

Identification of AAV serotypes for lung gene therapy in human embryonic stem cell-derived lung organoids
ανά: Meyer-Berg, H, κ.ά.
Έκδοση: (2020)

Identification of AAV serotypes for lung gene therapy in human embryonic stem cell-derived lung organoids
ανά: Helena Meyer-Berg, κ.ά.
Έκδοση: (2020-10-01)

Development of recombinant Adeno-Associated Viral vector (rAAV) for passive immunisation against ebola
ανά: Tan, T, κ.ά.
Έκδοση: (2017)

Homologous recombination mediates functional recovery of dysferlin deficiency following AAV5 gene transfer.
ανά: William E Grose, κ.ά.
Έκδοση: (2012-01-01)

Characterization of Recombinant Adeno-Associated Viruses (rAAVs) for Gene Therapy Using Orthogonal Techniques
ανά: Liam Cole, κ.ά.
Έκδοση: (2021-04-01)

Single-Step Purification/Solubilization of Recombinant Proteins: Application to Surfactant Protein B
ανά: Andreas Holzinger, κ.ά.
Έκδοση: (1996-05-01)

Efficient gene transduction in pigs and macaques with the engineered AAV vector AAV.GT5 for hemophilia B gene therapy
ανά: Yuji Kashiwakura, κ.ά.
Έκδοση: (2023-09-01)

Serotype-dependent recombinant adeno-associated vector (AAV) infection of Epstein–Barr virus-positive B-cells, towards recombinant AAV-based therapy of focal EBV + lymphoproliferative disorders
ανά: Elham Ahmadi, κ.ά.
Έκδοση: (2021-11-01)

Current Challenges and Future Directions in Recombinant AAV-Mediated Gene Therapy of Duchenne Muscular Dystrophy
ανά: Shin'ichi Takeda, κ.ά.
Έκδοση: (2013-06-01)

An AAV-Based NF-κB-Targeting Gene Therapy (rAAV-DMP-miR533) to Inflammatory Diseases
ανά: Luo T, κ.ά.
Έκδοση: (2022-06-01)

Optimized riboswitch-regulated AAV vector for VEGF-B gene therapy
ανά: Reetta A. E. Eriksson, κ.ά.
Έκδοση: (2022-12-01)

Immunogenicity and toxicity of AAV gene therapy
ανά: Hildegund C. J. Ertl
Έκδοση: (2022-08-01)

AAV gene therapy vectors in the TMJ
ανά: Sabine M. Brouxhon, κ.ά.
Έκδοση: (2022-12-01)

Allometric-like scaling of AAV gene therapy for systemic protein delivery
ανά: Alexandra Burr, κ.ά.
Έκδοση: (2022-12-01)

Assessment of toxicity and biodistribution of recombinant AAV8 vector–mediated immunomodulatory gene therapy in mice with Pompe disease
ανά: Gensheng Wang, κ.ά.
Έκδοση: (2014-01-01)

Establishment of mouse model of inherited PIGO deficiency and therapeutic potential of AAV-based gene therapy
ανά: Ryoko Kuwayama, κ.ά.
Έκδοση: (2022-06-01)

Safety and efficacy of an engineered hepatotropic AAV gene therapy for ornithine transcarbamylase deficiency in cynomolgus monkeys
ανά: Julien Baruteau, κ.ά.
Έκδοση: (2021-12-01)

Probing recombinant AAV capsid integrity and genome release after thermal stress by mass photometry
ανά: Eduard H.T.M. Ebberink, κ.ά.
Έκδοση: (2024-09-01)

Variation in the surfactant protein B gene is associated with development of emphysema in alpha 1 anti-trypsin deficiency
ανά: Wood, A, κ.ά.
Έκδοση: (2007)

Lentiviral gene therapy for the treatment of ABCA3-mediated surfactant deficiency
ανά: Ruffle, AR
Έκδοση: (2024)

Adding recombinant AAVs to the cancer therapeutics mix
ανά: Patrick L. Mulcrone, κ.ά.
Έκδοση: (2022-12-01)

The Role of Recombinant AAV in Precise Genome Editing
ανά: Swati Bijlani, κ.ά.
Έκδοση: (2022-01-01)

Gene Transfer in Rodent Nervous Tissue Following Hindlimb Intramuscular Delivery of Recombinant Adeno-Associated Virus Serotypes AAV2/6, AAV2/8, and AAV2/9
ανά: Asad Jan, κ.ά.
Έκδοση: (2019-11-01)

Corrigendum: Optimized riboswitch-regulated AAV vector for VEGF-B gene therapy
ανά: Reetta A. E. Eriksson, κ.ά.
Έκδοση: (2023-03-01)

Corrigendum to âAssessment of toxicity and biodistribution of recombinant AAV8 vectorâmediated immunomodulatory gene therapy in mice with Pompe diseaseâ
ανά: Gensheng Wang, κ.ά.
Έκδοση: (2015-01-01)

Editorial: Immunogenicity and toxicity of AAV gene therapy
ανά: Allison Bradbury, κ.ά.
Έκδοση: (2023-06-01)

Editorial: “AAV Gene Therapy: Immunology and Immunotherapeutics”
ανά: José M. Martinez-Navio, κ.ά.
Έκδοση: (2021-12-01)

Difficulties in the treatment of an infant survivor with inherited surfactant protein-B deficiency in Tunisia
ανά: Samia Hamouda, κ.ά.
Έκδοση: (2022-01-01)

Inclusion of PF68 surfactant improves stability of rAAV titer when passed through a surgical device used in retinal gene therapy
ανά: Patrício, M, κ.ά.
Έκδοση: (2019)

Inclusion of PF68 Surfactant Improves Stability of rAAV Titer when Passed through a Surgical Device Used in Retinal Gene Therapy
ανά: Maria I. Patrício, κ.ά.
Έκδοση: (2020-06-01)

Robust AAV Genotyping Based on Genetic Distances in Rep Gene That Are Maintained by Ubiquitous Recombination
ανά: Marina I. Beloukhova, κ.ά.
Έκδοση: (2022-05-01)

AAV-based gene replacement: The promise of gene therapy for deafness
ανά: Jieyu Qi, κ.ά.
Έκδοση: (2024-06-01)

Rational Design of AAV-rh74, AAV3B, and AAV8 with Limited Liver Targeting
ανά: Christopher Chan, κ.ά.
Έκδοση: (2023-10-01)

Optimizing an AAV-CRISPR system for retinal gene therapy
ανά: Stevanovic, M
Έκδοση: (2019)

Choroideremia: molecular mechanisms and development of AAV gene therapy
ανά: Patrício, M, κ.ά.
Έκδοση: (2018)

Progress of gene therapy based on AAV inhereditary deafness
ανά: Qi Jieyu, κ.ά.
Έκδοση: (2021-06-01)

AAV for Gene Therapy in Ocular Diseases: Progress and Prospects
ανά: Xiaoyu He, κ.ά.
Έκδοση: (2023-01-01)